MELAS Spectrum Disorders and Sonlicromanol: Progress Update

March 18, 2022 00:52:51
MELAS Spectrum Disorders and Sonlicromanol: Progress Update
MitoAction Expert Series
MELAS Spectrum Disorders and Sonlicromanol: Progress Update

Mar 18 2022 | 00:52:51

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Show Notes

Join MitoAction and Dr. Jan Smeitink, CEO of Khondrion for our our March Expert Series presentation. MELAS spectrum (m.3243A>G) disorders belong to the most frequently encountered group of primary mitochondrial diseases with an unmet medical need for treatment development. Following an introduction of the clinical disease spectrum Dr. Smeitink will discuss the development and state-of-art of Khondrion’s lead product sonlicromanol.

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